(at the Children's Hospital of Philadelphia)

The Hereditary Disease Foundation focuses on curing Huntington's disease (HD), a genetic brain disorder caused by a mistake in a single gene. This mistake is the same in all families worldwide with HD, so treatments and cures are expected to benefit everyone with the disease worldwide.

As a single gene disorder, Huntington's disease is an ideal model for other brain disorders

- a pathfinder. If scientists can understand what goes wrong in HD, it could help them understand aspects of many other neurodegenerative diseases, such as Alzheimer's, Parkinson's, and Lou Gehrig's disease. Treatments and cures developed for one disease could help guide the development of treatments for others.

The Hereditary Disease Foundation facilitates pivotal research by leading scientists towards identifying a cure. We organize collaborative scientific workshops, fund innovative research projects, and bring together international scientists to share their findings at our "Milton Wexler Celebration of Life" biennial symposium. Your support makes our work possible.